RobertMDS Patient

The Right Expression Can Change a Life

When genes are expressed at the wrong time or in the wrong amounts, it alters the function of a cell, leading to disease. By developing small-molecule medicines to control the expression of genes, we aim to make a profound difference in patients’ lives. We are advancing a growing pipeline of investigational medicines for diseases that have largely eluded other genomics-based approaches. Our current focus is on cancer and monogenic diseases.

Interested in Participating in a Clinical Trial?

If you’re interested in participating in a clinical trial, check to see if a trial is open near your area and if you meet the requirements to participate.

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Partnership Opportunities

We seek partnerships that maximize value for us and our partners by extending the potential of our gene control platform across multiple therapeutic areas and diseases.

View Our Partnership Focus

Our Publications and Abstracts

Learn more about the science and data behind our platform and our programs.

Read Publications and Abstracts